Nobel Prize for Medicine 2019

by Lauren Johnstone



This year the Nobel Prize for Physiology or Medicine was jointly awarded to William Kaelin of Harvard University, Peter Ratcliffe of Oxford University, and Gregg Semenza of Johns Hopkins University “for their discoveries of how cells sense and adapt to oxygen availability”.

It has long been known that oxygen is essential for life, but oxygen levels can vary as a result of altitude, exercise or disruption in blood supply caused by disease. Cells have adapted to respond to these changes. However, the molecular mechanism underlying how cells adapt was previously unknown before the work of these Nobel Laureates.

The body has many physiological adaptions to hypoxia (low oxygen levels). One such response is the increase in levels of the hormone erythropoietin (EPO) which in turn leads to a rise in the production of red blood cells. In order to gain an understanding of how this process was regulated by oxygen, Gregg Semenza studied the EPO gene. He was able to identify a specific region of the gene which was shown to mediate the response to hypoxia and a protein complex (HIF) which bound to the segment. HIF (hypoxia-inducible factor) was found to be made up of two transcription factors (proteins which regulate the rate of transcription of DNA to mRNA), HIF-1α and ARNT. HIF-1α was found to respond to oxygen levels. At high oxygen levels it was not present, but at low levels it was. This meant at low oxygen levels transcription of the EPO gene increased, thus increasing the amount of the hormone produced.  

Ratcliffe and Kaelin identified the VHL protein that is involved in destroying the HIF-1α protein at normal oxygen levels. Under normal oxygen levels the HIF-1α protein is modified by adding hydroxyl groups (this protein modification is called propyl hydroxylation). This allows VHL to recognise and bind to HIF-1α. The VHL protein is part of a complex which labels the HIF-1α with ubiquitin, which acts as a tag marking the protein for degradation in the proteasome.


The molecular switch revealed by these Laureates is important in helping us to understand and treat a variety of diseases. For example, the research has implications for patients with diseases where oxygen is in short supply such as anaemia, heart attacks and strokes. 

It also has implications for cancer research and treatment, as cancer cells have been shown to have increased levels of the HIF-1α protein in response to low oxygen levels. As a result, drugs that inhibit that protein can help treat cancer. At present a drug based on the prizewinning work is already being used to treat some cancers.


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